XXIII International Conference on Duchenne and Becker Muscular Dystrophy

Описание: ✨ The Conference continues on Friday afternoon at the 23rd Edition of the International Conference organized by Parent Project APS.
An intense afternoon where research, empowerment, and participation come together in an ongoing dialogue between clinical practice, personal experiences, and the community.
🔎 Patient experience data – Parent Project’s contribution to the EMA reflection paper, presented by Fernanda De Angelis, highlighting the value of patient experience data in European regulatory processes.
🤝 Empowerment in action: alliances between clinical and psycho-social experiences for an active life – A round table putting collaboration at the center, between healthcare professionals, associations, and people living with DMD and BMD, to create truly shared pathways.
🔬 A look at research – A scientific session on innovative perspectives, including Cell-Mediated Exon Skipping by Giulio Cossu (University of Manchester) and the selection of the best scientific posters, showcasing the work of the next generation of researchers.
🧬 Exon Skipping – With Annemieke Aartsma-Rus (Leiden University Medical Center) and Stefano Previtali (Ospedale San Raffaele), exploring one of the most studied therapeutic approaches for DMD.
🔄 Transition in DMD – A focus on a delicate and essential stage of care, with contributions from Rosaline Quinlivan (University College London) and Alessia Marcassoli (Istituto Neurologico Carlo Besta).
An afternoon that reflects the spirit of the Conference: scientific knowledge, listening, participation, and shared building.
We look forward to seeing you live tomorrow to continue this journey together.